A Dalmatian called Dino has become a viral sensation on social media for his small stuature. The dog has dwarfism condition, ...

Much of Josie’s confidence in navigating adolescence as a little person is thanks to her involvement with Little People of ...

BridgeBio said it received breakthrough therapy designation from the U.S. Food and Drug Administration for infigratinib, a treatment under development for children with achondroplasia. The ...

Oppenheimer has launched its coverage of BridgeBio Pharma (NASDAQ:BBIO) with a Perform recommendation, noting "substantial challenges" to the company as it races to market its late-stage assets, ...

The group of Jürgen Knoblich at the Institute of Molecular Biotechnology (IMBA) of the Austrian Academy of Sciences, has ...

(RTTNews) - BioMarin Pharmaceutical Inc. (BMRN), Wednesday announced positive data from the CANOPY clinical program evaluating Voxzogo in children with achondroplasia, a rare genetic skeletal ...

Summary study results show Ascendis’ drug for achondroplasia could be competitive to BioMarin's Voxzogo, which is the foundation of the latter company's growth plans.

(RTTNews) - Ascendis Pharma A/S (ASND) Monday said the pivotal ApproaCH study of TransCon CNP, in children with achondroplasia met its primary goal. The company's shares were more than 17 percent up ...

BioMarin stock dips in response to TransCon CNP data, as analysts note TransCon CNP could challenge BioMarin's Voxzogo by ...

For the primary endpoint of AGV at Week 52, children treated with TransCon CNP (n=57) demonstrated an LS mean AGV of 5.89 ...

Bhavya Johari will receive these gold medals at the NALSAR's 21st annual convocation from the President Droupadi Murmu ...

Last week, Ascendis Pharma A/S (NASDAQ:ASND) released topline data on Monday from a trial that included 84 children with ...