The drug is the only treatment available for the debilitating and progressive condition, and works by replacing the N-acetylgalactosamine-6-sulfatase enzyme lacking in people with the disease.

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To demonstrate how this can work, Andersson pointed to results from a study into the targeted delivery of a promising liver-targeted N-acetylgalactosamine (GalNAc) conjugated antisense ...

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1 College of Animal Science and Technology, Gansu Agricultural University, Lanzhou, China 2 College of Biological and Architectural Engineering, Baoji Vocational and Technical College, Baoji, China ...

Identification of potent COVID-19 main protease inhibitors by loading of favipiravir on Mg12O12 and Zn12O12 nanoclusters: an in silico strategy for COVID-19 treatment.

to N-acetylglucosamine to N-acetylgalactosamine ratio (GCST90200733), isoleucine to phosphate ratio (GCST90200868) were associated with a decreased risk for LAS. Sphingomyelin (d17:1/16:0, d18:1/15:0, ...

GalNAc, or N-acetylgalactosamine, a type of sugar molecule, is used by RNA-interference drug developers e.g., Alnylam Pharmaceuticals, Inc. (ALNY) in several of its approved drugs that target ...