Bhavya Johari will receive these gold medals at the NALSAR's 21st annual convocation from the President Droupadi Murmu ...

A Dalmatian called Dino has become a viral sensation on social media for his small stuature. The dog has dwarfism condition, ...

Josie Tang Tsz-kwan was born with achondroplasia, the most common form of short-limbed dwarfism. People with this condition ...

Much of Josie’s confidence in navigating adolescence as a little person is thanks to her involvement with Little People of ...

(RTTNews) - BioMarin Pharmaceutical Inc. (BMRN), Wednesday announced positive data from the CANOPY clinical program evaluating Voxzogo in children with achondroplasia, a rare genetic skeletal ...

Last week, Ascendis Pharma A/S (NASDAQ:ASND) released topline data on Monday from a trial that included 84 children with ...

(RTTNews) - Ascendis Pharma A/S (ASND) Monday said the pivotal ApproaCH study of TransCon CNP, in children with achondroplasia met its primary goal. The company's shares were more than 17 percent up ...

The FDA has granted Breakthrough Therapy Designation for oral infigratinib (BridgeBio Pharma), which is currently under development for children with achondroplasia, according to a press release from ...

BioMarin currently offers the only approved drug in the USA for achondroplasia, Voxzogo (vosoritide). All the news that moves ...

Ascendis Pharma A/S (NASDAQ:ASND) released topline data on Monday from a trial that included 84 children with achondroplasia, ...

BridgeBio Pharma BBIO) stock received a Perform rating from Oppenheimer on market challenges to its late-stage assets acoramidis and infigratinib. Read more here.

Predictably, weekly vs. daily subcutaneous injections made a big difference in the achondroplasia space, where shares of Copenhagen, Denmark-based Ascendis Pharma A/S (NASDAQ:ASND) closed Sept. 16 at ...