RCCS San Raffaele Scientific Institute in Milan researchers have discovered that hematopoietic stem cells (HSCs) adapt their lineage commitment during gene therapy based on the underlying genetic ...
Its first approved product, Casgevy, was developed in collaboration with narrow-moat Vertex Pharmaceuticals to treat transfusion-dependent beta-thalassemia (TDT) and sickle-cell disease (SCD). Crispr ...
New Delhi: Thalassemia patients at Delhi’s government hospitals are grappling with a “double whammy” amid a shortage of Desferal (deferoxamine mesylate) and a looming 50 percent price hike for the ...